Scientists are testing a new potential treatment for a rare neurodegenerative disorder. The inherited disorder, pantothenate kinase-associated neurodegeneration (PKAN), affects approximately 3 million people.
Researchers at St. Jude Children’s Research Hospital developed a compound that helps the body increase production of the molecule that, when in short supply, triggers PKAN. There is currently no treatment for PKAN. Clinical trials are in the planning stages.